The nuts and bolts of gene therapy for FSHD (Part 1 of 2)

https://is1-ssl.mzstatic.com/image/thumb/Podcasts126/v4/fb/22/6e/fb226e19-eefb-a965-c00c-669e7d76ec65/mza_14782204608570097893.jpg/600x600bb.jpg

MyFSHD

Peter L Jones, PhD

106 episodes

1 week ago

MyFSHD is about education and personal empowerment for the worldwide facioscapulohumeral muscular dystrophy (FSHD) community. Here we have discussions and commentary hosted by FSHD researcher Peter Jones, PhD, on many things of interest to the FSHD community. Learn about the science behind the different FSHD therapeutic approaches, FSHD pathology, family genetics and FSHD diagnostics. We will discuss upcoming clinical trials and what to look forward to. You will get to understand how you can be better prepared, become involved, and help contribute to defeating FSHD once and for all.

Non-Profit

Business

RSS

All content for MyFSHD is the property of Peter L Jones, PhD and is served directly from their servers with no modification, redirects, or rehosting. The podcast is not affiliated with or endorsed by Podjoint in any way.

Non-Profit

Business

https://d3t3ozftmdmh3i.cloudfront.net/staging/podcast_uploaded_episode/22295197/22295197-1755286173506-f4d4acb51106c.jpg

The nuts and bolts of gene therapy for FSHD (Part 1 of 2)

MyFSHD

1 hour 19 minutes 44 seconds

3 months ago

The nuts and bolts of gene therapy for FSHD (Part 1 of 2)

"My friends are toys. I make them. It's a hobby. I'm a genetic designer." This is a two part podcast covering the important factors is successful gene therapy and introduces the knowledge gained from other neuromuscular diseases and how it can be used to positively impact gene therapy in FSHD. In part 1, we focus on AAV serotypes, transgene constructs, immune responses, and delivery. We look into DMD gene therapy and how that can impact the current FSHD gene therapy programs. Check us out on the MyFSHD Youtube channel as well.