
This new episode on the Basic Science of Haemophilia Gene Therapy with Paul Batty introduces the science underlying this new therapy. Itprovides an overview of different gene therapy approaches, focussing on adeno-associated viral (AAV) vectors that are used for the treatment of haemophilia.
🎥 Watch the full module on the EAHAD Academy: https://academy.eahad.org/eahad/2024/module-10-basic-science-of-haemophilia-gene-thera/411461