Callum, Yasindhu & Aria, explore the ever-expanding world of gene therapy and gene editing. They investigate the gene therapy interventions for sickle cell patients and consider what this means for these patients going forward. Tune in to hear all about how gene therapy is already impacting lives!

References:

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[10] Ball, J., Bradley, A., Le, A., Tisdale, J.F. and Uchida, N. Current and future treatments for sickle cell disease: From hematopoietic stem cell transplantation to in vivo gene therapy. (2025). Mol Ther. 33(5), 2172-2191.

[11] Gray, V., Thomas, U., and Davies, K. (2024). Warrior Spirit: An Interview with Victoria Gray, Sickle Cell Pioneer. CRISPR J. 7(1), 5-11.